SNPMiner Trials by Shray Alag


SNPMiner Trials: Clinical Trial Report


Report for Clinical Trial NCT03672968

Developed by Shray Alag, 2019.
SNP Clinical Trial Gene

EAP Single Patient: Safety of Bilateral Intravitreal Injection of GS010 in a Single Subject Affected With G11778A ND4 Leber Hereditary Optic Neuropathy

Expanded Access Use for a single patient of Bilateral Intravitreal Injection of GS010 in a Single Subject Affected with G11778A ND4 Leber Hereditary Optic Neuropathy

NCT03672968 Leber Hereditary Optic Neuropathy (Optic, Atrophy, Hereditary, Leber)
MeSH: Atrophy Optic Nerve Diseases Optic Neuritis Optic Atrophy, Hereditary, Leber
HPO: Leber optic atrophy Optic neuritis Retrobulbar optic neuritis

1 Interventions

Name: GS010

Type: Genetic



There is one SNP

SNPs


1 G11778A

EAP Single Patient: Safety of Bilateral Intravitreal Injection of GS010 in a Single Subject Affected With G11778A ND4 Leber Hereditary Optic Neuropathy. --- G11778A ---

EAP_GS010_single Patient Expanded Access Use for a single patient of Bilateral Intravitreal Injection of GS010 in a Single Subject Affected with G11778A ND4 Leber Hereditary Optic Neuropathy The EAP applies to patients not eligible to ongoing GS010 clinical trials. --- G11778A ---

Inclusion Criteria: - Presence of documented G11778A ND4 LHON-causing mutation - Signature of informed consent and assent from the parent/guardian and the patient. --- G11778A ---

- Presence of known/documented mutations, other than the G11778A ND4 LHON-causing mutation, which are known to cause pathology of the optic nerve, retina or afferent visual system. --- G11778A ---



HPO Nodes


HPO:
Leber optic atrophy
Genes 11
COX3 CYTB ND1 ND2 TBC1D24 ND4 ND4L ATP6 ND5 ND6 CPLX1
Optic neuritis
Genes 19
HLA-B IL10 FAS ERAP1 IL12A IL12A-AS1 TK2 KLRC4 CCR1 UBAC2 C4A MEFV IL23R NLRC4 POLG NLRP3 STAT4 TLR4 NOD2
Retrobulbar optic neuritis
Genes 17
HLA-B IL10 FAS ERAP1 IL12A IL12A-AS1 KLRC4 CCR1 UBAC2 C4A MEFV IL23R NLRC4 NLRP3 STAT4 TLR4 NOD2